FDA approves Ionis' antisense drug as first targeted therapy for Alexander disease

Reports

12

Domains carrying it

12

First reported

3 September 2026

Latest report

5 September 2026

◆ Sectors

◆ Where

United States

◆ Timeline

1. 3 September 2026FDA Approves First Drug to Treat Alexander Diseasefda.gov
2. 4 September 2026ZANVASTRO™ (zilganersen) approved by the FDA as the first and only disease modifying ...ir.ionis.com
3. 5 September 2026Ionis Pharmaceuticals, Inc. (IONS) Discusses FDA Approval and Launch Strategy for ...seekingalpha.com
4. 5 September 2026Ionis Pharma'szilganersen receives US FDA approval for Alexander disease in paediatric ...pharmabiz.com

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◆ Share

◆ Evidence

12 reports · 12 domains

• Ionis Pharma'szilganersen receives US FDA approval for Alexander disease in paediatric ...pharmabiz.com · 5 September 2026
• What an Alexander Disease Approval Means for RNA Developerspharmtech.com · 5 September 2026
• Ionis Pharmaceuticals, Inc. (IONS) Discusses FDA Approval and Launch Strategy for ...seekingalpha.com · 5 September 2026
• FDA Approves Ionis Pharma Drug, the First for Ultra-Rare Alexander Diseasemedcitynews.com · 4 September 2026
• Rare Brain Disorder Gets Its First FDA Drug Approvalmedpagetoday.com · 4 September 2026
• FDA Approves Zanvastropharmexec.com · 4 September 2026
• Ionis' 'breakthrough' Alexander disease approval establishes pillar of rare disease pipelinefiercepharma.com · 4 September 2026
• FDA Approves Ionis ASO Zanvastro for Alexander Disease From Infancygenomeweb.com · 4 September 2026
• ZANVASTRO™ (zilganersen) approved by the FDA as the first and only disease modifying ...ir.ionis.com · 4 September 2026
• FDA approves Ionis' antisense drug as first targeted therapy for Alexander diseasebiospace.com · 3 September 2026
• FDA approves zilganersen (Zanvastro) as first treatment for Alexander diseasecontemporarypediatrics.com · 3 September 2026
• FDA Approves First Drug to Treat Alexander Diseasefda.gov · 3 September 2026