FDA Approves Gene Therapy for Glycogen Storage Disease Type 1a

Reports

6

Domains carrying it

6

First reported

19 August 2026

Latest report

22 August 2026

◆ Sectors

◆ Where

United States

◆ Timeline

1. 19 August 2026Ultragenyx's gene therapy wins first FDA approval for rare metabolic disorderreuters.com
2. 20 August 2026FDA Approves Gene Therapy for Glycogen Storage Disease Type 1ahcplive.com
3. 22 August 2026Ultragenyx Receives Accelerated FDA Approval For Metabolic Gene Therapyinsideprecisionmedicine.com

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◆ Share

◆ Evidence

6 reports · 6 domains

• Ultragenyx Receives Accelerated FDA Approval For Metabolic Gene Therapyinsideprecisionmedicine.com · 22 August 2026
• GSDIa Gene Therapy Approval Signals New Path for Rare Disease Manufacturingpharmtech.com · 20 August 2026
• FDA Approves Genglycos, First Gene Therapy for Glycogen Storage Disease Type 1awebmd.com · 20 August 2026
• FDA Approves First Gene Therapy for GSDIapharmacytimes.com · 20 August 2026
• FDA Approves Gene Therapy for Glycogen Storage Disease Type 1ahcplive.com · 20 August 2026
• Ultragenyx's gene therapy wins first FDA approval for rare metabolic disorderreuters.com · 19 August 2026