FDA approves Zanvastro, first drug to treat rare Alexander disease

The FDA has approved Zanvastro, the first drug to treat Alexander disease, a rare and life-threatening neurological disorder caused by protein buildup damaging the nervous system. The drug reduces the disease's root cause and offers the first therapeutic option beyond supportive care for patients from infancy to adulthood.

This Wire brief sits within Fusion42's coverage of Biotech, and 15 sources have reported it between 3 Sep 2026 and 22 Sep 2026.