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Ultragenyx Announces U.S. FDA Approval of GENGLYCOS™ Gene Therapy, the First-Ever ...
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Fusion42 · 19 August 2026 · Fusion42 review
U.S. FDA granted accelerated approval for Ultragenyx's GENGLYCOS™, the first-ever gene therapy targeting glycogen storage disease type Ia (GSDIa), providing a treatment that reduces reliance on cornstarch and mitigates hypoglycemia risk.
This Wire brief sits within Fusion42's coverage of Biotech, and 2 sources have reported it.
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You can now offer a transformative gene therapy to patients with GSDIa, bypassing the strict cornstarch regimen that shaped care for decades. This opens routes to engage providers who previously managed an untreatable ultra-rare disease.
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2 sources · 19 Aug 2026
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